Cell and gene therapy products

In recent years, cell and gene therapies have offered new and promising therapeutic modalities for the treatment of rare, inherited and acquired diseases. While both cell and gene therapies aim to introduce biological functions into the patient, the mechanisms in which they operate differ. Cell therapy involves the introduction or implantation of healthy cells as a whole to replace those that are diseased or missing. In gene therapy, the faulty gene is modified and normal function restored with the introduction of genetic material into targeted cells via viral or nonviral delivery. 

This Spotlight will explore the different bioanalytical tools utilzed to support cell and gene therapy development, different viral and nonviral vectors and the regulatory landscape for cell and gene therapies.

This feature was produced in association with Frontage Laboratories, Inc, Charles River Laboratories, Bio-Rad, PPD Laboratory Services and Bio-Techne.